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myotonic dystrophy

Synonyms

Noun

1. myotonic muscular dystrophy

2. myotonia atrophica, Steinert's disease, muscular dystrophy, dystrophy

Usage
Dialing Back Stiffness May Protect Muscles in Myotonic Dystrophy - University of Rochester
Myotonic Dystrophy Foundation Chair Jeremy Kelly Awarded OBE by King Charles III - EIN Presswire
An Antibody–Oligonucleotide Conjugate for Myotonic Dystrophy Type 1 - The New England Journal of Medicine
Source of gastrointestinal problems in myotonic dystrophy - National Institutes of Health (NIH) | (.gov)
Aberrantly spliced α-dystrobrevin alters α-syntrophin binding in myotonic dystrophy type 1 - Neurology® Journals
Targeted long-read sequencing for high-resolution repeat profiling in myotonic dystrophy type 1 - Nature
Undiagnosed Maternal Myotonic Dystrophy Type 1 Revealed by Congenital Myotonic Dystrophy in the Neonate - Cureus
Muscle disease - Myotonic, Dystrophy, Congenital - Encyclopedia Britannica
MDA 2026: Dyne therapy boosts strength, cognition in DM1 - Muscular Dystrophy News
ARTHEx Biotech Delivers Multiple Presentations at IDMC-15 Highlighting Clinical Progress of ATX-01 and Mechanistic Insights for Myotonic Dystrophy Type 1 (DM1) and 2 (DM2) - PR Newswire
Neonatal congenital myotonic dystrophy with DMPK gene expansion: clinical features and short-term outcomes - Frontiers
Toward Trial Readiness in Congenital Myotonic Dystrophy - Neurology® Journals
Myotonic dystrophy type 1: clinical diversity, molecular insights and therapeutic perspectives - Nature
Dyne hopes to bring new treatment for DM1 to US market in 2028 - Muscular Dystrophy News
Role of Otolaryngology in Monitoring the Progression of Myotonic Dystrophy: A Case Report - Cureus
AMO Pharma Announces Update on Scientific Advice for Registrational Clinical Study of AMO-02 in Congenital Myotonic Dystrophy Type 1 Following Meetings with the U.S. Food and Drug Administration, the U.K. Medicines and Healthcare products Regulator - PR Newswire
Prospective Study of Video Hand Opening Time as a Quantitative Measurement of Myotonia in Patients With Myotonic Dystrophy Type 1 - Neurology® Journals
Characterizing white matter hyperintensities in myotonic dystrophy type 1 through IVIM derived metrics - Nature
Breakthrough in RNA Research Could Lead to Treatment for Neuromuscular Disorders - Carnegie Mellon University
Pre- and postsynaptic upregulation of FasII synergistically underlies neuropathological and behavioral phenotypes in a Drosophila model of myotonic dystrophy - Nature
Sarepta Provides Progress Update for SRP-1003, its Investigational siRNA treatment for Myotonic Dystrophy Type 1 - Sarepta Therapeutics
Reducing Muscle Stiffness Could Help Myotonic Dystrophy Patients - Bioengineer.org
MBNL loss of function in smooth muscle as a model for myotonic dystrophy associated gastrointestinal dysmotility - PNAS
An antibody-siRNA conjugate could treat myotonic dystrophy - BioXconomy
PepGen Announces Presentations at the 15th International Myotonic Dystrophy Consortium Highlighting Clinical Data from the PGN-EDODM1 Program - Business Wire
2026 Grad Slam winner strives to understand sleep disruptions in myotonic dystrophy - Newsroom | UCLA
Safety and efficacy of novel antibody-oligonucleotide therapy for myotonic dystrophy type 1 - 2 Minute Medicine
Antibody-Oligonucleotide Conjugate Shows Promise in Myotonic Dystrophy Type 1 - MedPage Today
Myotonic dystrophy drug SRP-1003 trial advances to higher doses - Muscular Dystrophy News
PepGen’s Mid-Stage Myotonic Dystrophy Study Hit With ‘Surprise’ Pause - BioSpace
Over-contracted gut muscles drive gastrointestinal symptoms in myotonic dystrophy - News-Medical
ARTHEx Biotech Granted FDA Fast Track Designation for ATX-01 for the Treatment of Myotonic Dystrophy Type 1 (DM1) - PR Newswire
Therapeutic Promise and Mechanism of DYNE-101 to Treat Myotonic Dystrophy: Doug Kerr, MD, PhD - NeurologyLive
PepGen muscular dystrophy drug gets ‘surprise’ hold from FDA - BioPharma Dive
MDA 2026: Early trial of PGN-EDODM1 shows biomarker activity in DM1 - Muscular Dystrophy News
VCU and UAlbany earn $6.5M grant to launch a Wellstone muscular dystrophy center - VCU News
Miles of Hope: A year-long ride for Myotonic Dystrophy awareness - News 9
AMO-02 for myotonic dystrophy type 1 - Muscular Dystrophy News
New ‘pothole-filling’ RNA strategy targets the genetic root of DM1 - Muscular Dystrophy News
Sarepta Announces First Clinical Data from siRNA Pipeline Targeting FSHD1 and DM1 - Sarepta Therapeutics
Discovery and characterization of Arthex Biotech’s ATX-01 for myotonic dystrophy type 1 - BioWorld News
Dyne Therapeutics Announces Completion of Enrollment in Registrational Expansion Cohort of ACHIEVE Trial of Z-Basivarsen for Myotonic Dystrophy Type 1 (DM1) - Yahoo Finance
Early trial data support RNA therapies for two muscular dystrophy types - Muscular Dystrophy News
Researchers provide answers to progressive heart problems in muscular dystrophy and potential reversibility - Baylor College of Medicine Blog Network -
Gene Therapy Fast Tracked for Non-Congenital Myotonic Dystrophy Type 1 - Neurology Advisor
Dyne commences Phase III HARMONIA trial for DM1 therapy - Clinical Trials Arena
DM1 gene therapy trial seeks patients ages 10-50 - Muscular Dystrophy News
Sarepta CEO Doug Ingram To Step Down as Muscular Dystrophy Mission Hits Home - BioSpace
UAlbany, VCU to share $6.5M to Launch Muscular Dystrophy Research Center - University at Albany
Muscular Dystrophy Association Announces More Than $2.7 Million For Research Grants to Advance Breakthroughs Across Neuromuscular Diseases - Muscular Dystrophy Association
FDA Grants Fast Track Designation to SAR446268 Gene Therapy for Non-Congenital Myotonic Dystrophy Type 1 - Vera Health
Man stops in Tampa before finishing 200k miles on motorcycle for rare disease - Spectrum Bay News 9
PepGen Loses Half of Share Price on Mixed Data in Rare Muscle-Wasting Disease - BioSpace
Whitehall man rides 200K miles to raise money, awareness for myotonic muscular dystrophy - WFMZ.com
Mouse model reveals unsuspected effects of muscular dystrophy in the GI - Baylor College of Medicine Blog Network -
Development and Validation of a Disease-Specific, Patient-Reported Outcome Measure: The Myotonic Dystrophy Type 2 Health Index - Wiley Online Library
Structure-based RNA could lead to treatment for neuromuscular disorders - Medical Xpress
Del-desiran for myotonic dystrophy type 1 - Muscular Dystrophy News
Overviewing Positive Early Data from ACHIEVE Trial of Zeleciment Basivarsen in DM1: Doug Kerr, MD, PhD - NeurologyLive
The New England Journal of Medicine Publishes Results from Phase 1/2 MARINA® Trial of Delpacibart Etedesiran (del-desiran) for Treatment of Myotonic Dystrophy Type 1 - BioSpace
PepGen hit with partial clinical hold, analyst blames 'understaffed FDA' - Fierce Biotech
Novartis gets win for another Avidity muscular dystrophy AOC - pharmaphorum
Alternative Splicing of SORBS1 Affects Neuromuscular Junction Integrity in Myotonic Dystrophy Type 1 - Wiley Online Library
Dyne Therapeutics Receives Orphan Drug Designation in Japan for Zeleciment Basivarsen (DYNE-101) for Myotonic Dystrophy Type 1 - Yahoo Finance
AMO Pharma Announces Update on Scientific Advice for Registrational Clinical Study of AMO-02 in Congenital Myotonic Dystrophy Type 1 Following Meetings with the U.S. Food and Drug Administration, the U.K. Medicines and Healthcare products Regulator - Bennington Banner
AMO Pharma Reports Long-Term Safety Data from REACHCDM-X Study of AMO-02 in Treatment of Congenital Myotonic Dystrophy Type 1 - PR Newswire
Design Therapeutics begins DM1 trial for DT-818, aims at genetic cause - Stock Titan
Landmarks light up green for Myotonic Dystrophy Awareness Day - WRGB
AMO Pharma Announces Update on Scientific Advice for Registrational Clinical Study of AMO-02 in Congenital Myotonic Dystrophy Type 1 Following Meetings with the U.S. Food and Drug Administration, the U.K. Medicines and Healthcare products Regulator - The Journal Gazette
AMO Pharma Announces Update on Scientific Advice for Registrational Clinical Study of AMO-02 in Congenital Myotonic Dystrophy Type 1 Following Meetings with the U.S. Food and Drug Administration, the U.K. Medicines and Healthcare products Regulator - Colchester Sun
Myotonic Dystrophy Foundation Expanding Global Treatment - BORGEN Magazine
AMO Pharma Announces Update on Scientific Advice for Registrational Clinical Study of AMO-02 in Congenital Myotonic Dystrophy Type 1 Following Meetings with the U.S. Food and Drug Administration, the U.K. Medicines and Healthcare products Regulator - nny360.com
Experimental DM1 drug hits key trial milestone, Dyne eyes 2028 US launch - Stock Titan
PepGen Reports First Quarter 2026 Financial Results and Recent Corporate Highlights - Business Wire
CUHK scientists reveal a new mechanism by which myotonic dystrophy type 1 damages the nervous system - CUHK Communications and Public Relations Office
US FDA puts partial clinical hold on PepGen's muscle disease drug trial - Reuters
ARTHEx Biotech Upsizes Series B Financing Round to $87M to Advance Lead Program ATX-01 in Myotonic Dystrophy Type 1 and Expand Pipeline of Targeted RNA Medicines - PR Newswire
PepGen Announces Regulatory Updates on FREEDOM2 - Business Wire
After Mortality-Marred Year, Sarepta Looks Ahead to Catalyst-Rich 2026 - BioSpace
Dyne Therapeutics Initiates Phase 3 HARMONIA Trial to Evaluate Efficacy of Z-Basivarsen in Myotonic Dystrophy Type 1 - Quiver Quantitative
Sarepta shares positive safety update on DM1 asset as Arrowhead snares $200M milestone - Fierce Biotech
Smartphones match traditional methods in monitoring patients with muscular dystrophy - News-Medical
Three cases of pregnancies complicated with myotonic dystrophy type 1 - obgyn.onlinelibrary.wiley.com
PepGen’s stock up 120% on DM1 trial success - Clinical Trials Arena
FDA curtails Pepgen’s Freedom2 operate in DM1 - BioWorld News
News - New research could unlock ways to treat myotonic dystrophy - University of Nottingham
'Vroom Old Man' surpasses fundraising, distance goals in motorcycle ride for disease research - KCENTV.com
'Vroom Old Man' | One man's 200,000-mile motorcycle mission to fight rare disease - KCENTV.com
[8-K] PepGen Inc. Reports Material Event - Stock Titan
Dyne Therapeutics Reports Significant One-Year Clinical Data for Zeleciment Basivarsen in Patients with Myotonic Dystrophy Type 1 - Quiver Quantitative
Autism-related traits in myotonic dystrophy type 1 model mice are due to MBNL sequestration and RNA mis-splicing of autism-risk genes - Nature
Chronic endoplasmic reticulum stress in myotonic dystrophy type 2 promotes autoimmunity via mitochondrial DNA release - Nature
MDA 2024: Myotonic dystrophy type 1 reverses with AOC 1001 treatment - Muscular Dystrophy News
FDA puts PepGen’s Phase 2 muscle disease trial on partial hold - Endpoints News
ARTHEx Biotech: Series B Round Upsized To $87 Million For Myotonic Dystrophy Treatment Development - Pulse 2.0
Clearance of defective muscle stem cells by senolytics restores myogenesis in myotonic dystrophy type 1 - Nature
Myotonic dystrophy: GABA receptors implicated in sleepiness, via mouse model - Emory News
Implications of circular transcripts in DM1 pathomechanism - ScienceDirect.com
Myotonic Dystrophy Type 2 Caused by a CCTG Expansion in Intron 1 of ZNF9 - Science | AAAS
Molecular genetics of myotonic dystrophy and the evolution of therapeutic approaches | Journal of Human Genetics - Nature
Foreign Language Equivalents
Foreign Language Equivalents of 'myotonic dystrophy'
Language Equivalent   Language Equivalent
French    Spanish
Misspellings - Typos
myotonic dystrophhy,   myotoni dystrophy,   myotonic fystrophy,   myitonic dystrophy,   myotonic dystriphy,   myotonic systrophy,   mytoonic dystrophy,   muotonic dystrophy,   myotpnic dystrophy,   myotonc dystrophy,   myyotonic dystrophy,   myotonic dystroohy,   myotonic dystropyh,   myotonic dystrrophy,   myotonic dystropy,   myotonic dystorphy,   myotonic dysrophy,   myotonic dyatrophy,   moytonic dystrophy,   myotonic dystrophy,   myotonic dystrpphy,   yotonic dystrophy,   myotonic dystophy,   myoronic dystrophy,   myotonic dystropgy,   myotonic dystropphy,   myotonic dsytrophy,   myottonic dystrophy,   myotoinc dystrophy,   myotonic dyystrophy,   myootnic dystrophy,   myotoniic dystrophy,   myotonic dystrphy,   myotnoic dystrophy,   myotonic dystrohpy,   myoonic dystrophy,   myotoonic dystrophy,   myotonic dystrophyy,   mytonic dystrophy,   myotonic dystrophu,   myotonic dysteophy,   myotonicd ystrophy,   myotinic dystrophy,   myotonic dysrtophy,   myotonic dysstrophy,   myotonic dydtrophy,   myptonic dystrophy,   myotomic dystrophy,   myotonic dysrrophy,   myotobic dystrophy,   myotonic dtstrophy,   myotoic dystrophy,   myotonuc dystrophy,   myotonic dystrohy,   myootonic dystrophy,   myotonix dystrophy,   mtotonic dystrophy,   myotonic ystrophy,   myotonic dystropjy,   myotonci dystrophy,   myotonic dstrophy,   myotonic dustrophy,   myotonic dytrophy,   myotnic dystrophy,   motonic dystrophy,   myotonicdystrophy,   ,yotonic dystrophy,   myotonic dytsrophy,   myotonic dysttophy,   myotoniv dystrophy,   myotonic dystroph,   myotonic dystroophy,   myotonicc dystrophy,   myotonic dysttrophy,   myotonic ydstrophy,   myotonic dystropht,   myotonic ddystrophy,   myotonoc dystrophy,   myotonic dystrpohy,   mmyotonic dystrophy,   nyotonic dystrophy,   ymotonic dystrophy,   myotonic dysyrophy,   myotoni cdystrophy,   myotonnic dystrophy,   myotonic dystro[hy,   myoyonic dystrophy
Words Starting with Letter - 'A'
a a battery a billion
a bit a bit much a capella singing
a cappella singing a couple of a few
a fortiori a good deal a great deal
a horizon a hundred a hundred and one
a hundred thousand a hundred times a kempis
a la carte a la mode a level
a little a lot a million
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